{"id":10486,"date":"2022-11-15T21:16:21","date_gmt":"2022-11-15T21:16:21","guid":{"rendered":"https:\/\/latam.ptcbio.com\/pt\/?page_id=717"},"modified":"2025-10-09T15:44:47","modified_gmt":"2025-10-09T19:44:47","slug":"ptc-therapeutics","status":"publish","type":"page","link":"https:\/\/latam.ptcbio.com\/pt\/","title":{"rendered":"P\u00e1gina Inicial"},"content":{"rendered":"<div class=\"hero-header__outer-container\">\n\n\t<div class=\"hero hero--styled color-theme--red-gradient hero--has-image hero--normal-spacing\">\n\t\t\t\t\t\t<div class=\"hero__bg\">\n\t\t\t<div id=\"particles-js\" class=\"hero__constellation hero__constellation--left\"><\/div>\n\t\t<\/div>\n\t\t\t\t\t\t\t\t<div class=\"hero__inner hero__inner--left\">\n\t\t\t<div class=\"hero__content hero__content--left hero__content--has-image\">\n\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"hero__eyebrow\">Traduzindo ci\u00eancia<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"u-mt-1 u-my-2\"><h1 class=\"hero__title hero__title--standard\" data-ptc-fitty=\"\">Transformando vidas<\/h1><\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"hero__subtitle\">Desenvolvendo terapias transformadoras \u00e0s crian\u00e7as e aos adultos com doen\u00e7as graves e necessidades m\u00e9dicas ainda n\u00e3o atendidas.<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t<figure class=\"hero__image-wrapper hero__image-wrapper--left\">\n\t\t\t\t\t\t\t\t\t<figcaption class=\"hero__figcaption\">\n\t\t\t\t\t\t<span id=\"hero-image-caption\" class=\"hero__caption js-hidden\"><\/span><br>\n\t\t\t\t\t\t<span id=\"hero-image-subcaption\" class=\"hero__subcaption js-hidden\"><\/span>\n\t\t\t\t\t<\/figcaption>\n\t\t\t\t\t<img decoding=\"async\" id=\"hero-image-people\" src=\"data:image\/svg+xml,%3Csvg xmlns='http:\/\/www.w3.org\/2000\/svg'\/%3E\" alt=\"\" class=\"hero__image js-hidden\" data-files='[{\"url\":\"https:\\\/\\\/latam.ptcbio.com\\\/pt\\\/wp-content\\\/uploads\\\/sites\\\/10\\\/2025\\\/08\\\/DSC_1088.webp\",\"alt\":\"Brittany\",\"caption\":\"Brittany\",\"subcaption\":\"Paciente de ataxia de Friedreich, Canad\\u00e1\"},{\"url\":\"https:\\\/\\\/latam.ptcbio.com\\\/pt\\\/wp-content\\\/uploads\\\/sites\\\/10\\\/2025\\\/08\\\/Evonne-600.png\",\"alt\":\"Evonne\",\"caption\":\"Evonne\",\"subcaption\":\"Paciente de doen\\u00e7a de Huntington, Estados Unidos\"},{\"url\":\"https:\\\/\\\/latam.ptcbio.com\\\/pt\\\/wp-content\\\/uploads\\\/sites\\\/10\\\/2025\\\/08\\\/raul600.png\",\"alt\":\"Raul\",\"caption\":\"Raul\",\"subcaption\":\"Paciente de Duchenne, Brasil\"},{\"url\":\"https:\\\/\\\/latam.ptcbio.com\\\/pt\\\/wp-content\\\/uploads\\\/sites\\\/10\\\/2025\\\/08\\\/Pam-and-Kelsey.png\",\"alt\":\"Pam and Kelsey\",\"caption\":\"Pam &amp; Kelsey\",\"subcaption\":\"Paciente de fenilceton\\u00faria, Estados Unidos\"},{\"url\":\"https:\\\/\\\/latam.ptcbio.com\\\/pt\\\/wp-content\\\/uploads\\\/sites\\\/10\\\/2025\\\/08\\\/V3.png\",\"alt\":\"Simone\",\"caption\":\"Simone\",\"subcaption\":\"Paciente de defici\\u00eancia de AADC, It\\u00e1lia\"}]'>\n\t\t\t\t\t\t\t\t\t<\/figure>\n\t\t\t\t\t<\/div>\n\t\t\t<\/div>\n\t\t\t<div class=\"hero__breadcrumbs\"><nav\n\tclass=\"breadcrumbs breadcrumbs--shallow\"\n\taria-label=\"Breadcrumb\"\n>\n\t<ol class=\"breadcrumbs__list\" itemscope itemtype=\"https:\/\/schema.org\/BreadcrumbList\">\n\t\t\t\t\t\t\t\t\t<li class=\"breadcrumbs__crumb breadcrumbs__crumb--light\" itemscope itemprop=\"itemListElement\" itemtype=\"https:\/\/schema.org\/ListItem\">\n\t\t\t\t\t\t\t\t\t\t\t<a class=\"breadcrumbs__link breadcrumbs__link--home breadcrumbs__link--light\" itemprop=\"item\" href=\"https:\/\/latam.ptcbio.com\/pt\/\">\n\t\t\t\t\t\t\t<span class=\"sr-only\" itemprop=\"name\">P\u00e1gina Inicial<\/span>\n\t\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t\t\t\t<meta itemprop=\"position\" content=\"1\" \/>\n\t\t\t\t<\/li>\n\t\t\t\t\t\t\t\t\t\t\t<\/ol>\n<\/nav>\n<\/div>\n\t<\/div>\n\n\n<div  class=\"text-block text-block--standard color-theme--white\">\n\t\t<div class=\"text-block__wrapper\" >\n\n\t\t\n\t\t\t\t\t<h2 class=\"text-block__heading\">\n\t\t\t\t<span class=\"heading--2\"  data-ptc-fitty=\"\">Inova\u00e7\u00e3o movida pela ci\u00eancia e pela paix\u00e3o aos pacientes<\/span>\n\t\t\t<\/h2>\n\t\t\n\t\t<div class=\"text-block__content wysiwyg--decoration wysiwyg--color\">\n\t\t\t<p><span data-contrast=\"auto\">A PTC \u00e9 uma empresa biofarmac\u00eautica global focada na descoberta, no desenvolvimento e na comercializa\u00e7\u00e3o de terapias transformadoras para crian\u00e7as e adultos que vivem com doen\u00e7as raras. H\u00e1 25 anos, utilizamos nossas plataformas cient\u00edficas para tratar a causa raiz dessas condi\u00e7\u00f5es e concretizar nossa promessa: proporcionar mais momentos para quem confia em n\u00f3s.<\/span><span data-ccp-props=\"{}\">\u00a0<\/span><\/p>\n<p><span data-contrast=\"auto\">Atualmente, a empresa est\u00e1 presente em mais de 50 pa\u00edses ao redor do mundo. Na Am\u00e9rica Latina, em cerca de 15 pa\u00edses. Em 2015, o Brasil foi o primeiro a receber a PTC Therapeutics, seguido da Argentina.<\/span><\/p>\n\t\t<\/div>\n\n\t\t\n\t\t\t<div class=\"dual-cta__ctas dual-cta__ctas--same dual-cta__ctas--center\">\n\n\t\t\t\t\t<a href=\"https:\/\/latam.ptcbio.com\/pt\/nossa-ciencia\/\" target=\"\" class=\"dual-cta__button text-cta text-cta--secondary\">Conhe\u00e7a a nossa ci\u00eancia<\/a>\n\t\t\n\t\t\n\t\t\n\t<\/div>\n\n\t<\/div>\n<\/div>\n\n\n\n<div  class=\"two-up container--max-width color-theme--white\">\n\t\t\t<div class=\"two-up__heading\" style=\"--ptc--heading--bg: var(--wp--preset--color--reddish );\" >\n\t\t\t<span>\n\t\t\t\t<h2 class=\"two-up__heading-text heading--2\" data-ptc-fitty=\"\">Nossas plataformas cient\u00edficas<\/h2>\n\t\t\t<\/span>\n\t\t<\/div>\n\t\n\t<div class=\"two-up__blocks two-up__blocks--2 two-up__blocks--top\" style=\"--ptc--2up-cols:2\" >\n\t\t\t\t\t\n\t\t\t<div class=\"two-up__block two-up__block--dashicons \">\n\t\t\t\t\t\t\t\t\t\t\t\t\t<img decoding=\"async\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/themes\/ptc-redesign\/images\/splicing-dna.svg\" alt=\"\" class=\"two-up__block__icon two-up__block__icon--static\">\t\t\t\t\t\t\t\t<div class=\"two-up__block-wrapper\">\n\t\t\t\t\t\t\t\t\t\t<div class=\"two-up__block__title\">\n\t\t\t\t\t\t<span class=\"heading--4\" data-ptc-fitty=\"\">Splicing<\/span>\n\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t<div class=\"two-up__block__text body-copy--2\">\n\t\t\t\t\t\tModula\u00e7\u00e3o do processo de splicing para controlar a produ\u00e7\u00e3o de prote\u00ednas.\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<a href=\"https:\/\/latam.ptcbio.com\/pt\/nossa-ciencia\/splicing\/\" target=\"_self\" class=\"two-up__block__link text-cta text-cta--secondary\">Saiba mais<\/a>\n\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t<\/div>\n\t\t\t\t\t\n\t\t\t<div class=\"two-up__block two-up__block--dashicons \">\n\t\t\t\t\t\t\t\t\t\t\t\t\t<img decoding=\"async\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/themes\/ptc-redesign\/images\/inflammation-ferroptosis.svg\" alt=\"\" class=\"two-up__block__icon two-up__block__icon--static\">\t\t\t\t\t\t\t\t<div class=\"two-up__block-wrapper\">\n\t\t\t\t\t\t\t\t\t\t<div class=\"two-up__block__title\">\n\t\t\t\t\t\t<span class=\"heading--4\" data-ptc-fitty=\"\">Inflama\u00e7\u00e3o &amp; Ferroptose<\/span>\n\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t<div class=\"two-up__block__text body-copy--2\">\n\t\t\t\t\t\tA\u00e7\u00e3o sobre vias de estresse oxidativo e inflama\u00e7\u00e3o para tratar doen\u00e7as do sistema nervoso central.\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<a href=\"https:\/\/latam.ptcbio.com\/pt\/nossa-ciencia\/inflamacao-e-ferroptose\/\" target=\"_self\" class=\"two-up__block__link text-cta text-cta--secondary\">Saiba mais<\/a>\n\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t<\/div>\n\t\t\t<\/div>\n<\/div>\n\n\n<svg  class=\"wave-transition\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" viewBox=\"0 0 2560 168\" style=\"color:var(--wp--preset--color--white);\">\n\t<path fill=\"var(--wp--preset--color--purple-steel)\" d=\"M2560,168.25V.25C1941.9-6.65,1329.6,131.45,726,95.25S0,.25,0,.25V168.25H2560Z\"\/>\n<\/svg>\n\n\n\t<div  class=\"three-up-slider color-theme--purple-steel\">\n\n\t\t\t\t\t<div\n\t\t\t\t\t\t\t\tclass=\"three-up-slider__subheading heading--6\"\n\t\t\t\t\t\t\t>\n\t\t\t\t\u00c1reas terap\u00eauticas\t\t\t<\/div>\n\t\t\n\t\t\t\t\t<h3 class=\"three-up-slider__heading heading--2\" >\n\t\t\t\tDoen\u00e7as em foco\t\t\t<\/h3>\n\t\t\n\t\t\t\t<div role=\"group\" aria-roledescription=\"carousel\" data-splide-per-page=\"3\" class=\"splide splide--dark\" >\n\t\t\t<div class=\"splide__arrows\" data-slide-count=\"7\">\n\t\t\t\t<button class=\"splide__arrow splide__arrow--prev\">\n\t\t\t\t\t<span class=\"sr-only\">Go to previous slide<\/span>\n\t\t\t\t\t<i class=\"icon-caret-left\"><\/i>\n\t\t\t\t<\/button>\n\t\t\t\t<button class=\"splide__arrow splide__arrow--next\">\n\t\t\t\t\t<span class=\"sr-only\">Go to next slide<\/span>\n\t\t\t\t\t<i class=\"icon-caret-right\"><\/i>\n\t\t\t\t<\/button>\n\t\t\t<\/div>\n\t\t\t<div class=\"splide__track\">\n\t\t\t\t<div class=\"three-up-slider__slides splide__list\">\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide splide__slide\">\n\t\t\t\t\t\t\t<a href=\"https:\/\/latam.ptcbio.com\/pt\/areas-terapeuticas\/fenilcetonuria\/\" target=\"_self\" class=\"splide__slide__container\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-image\">\n\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"400\" height=\"396\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/Pam-and-Kelsey-400x396.png\" class=\"attachment-three-up-slider size-three-up-slider\" alt=\"PKU Patient\" sizes=\"auto,(min-width: 1920px) calc(1440px \/ 3), (min-width: 1440px) calc(1380px \/ 3), (min-width: 1200px) calc(1140px \/ 3), (min-width: 900px) calc(860px \/ 3), (min-width: 768px) calc(720px \/ 3), (min-width: 600px) calc(540px \/ 2), calc(100vw \/ 1)\" srcset=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/Pam-and-Kelsey-400x396.png 400w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/Pam-and-Kelsey-300x297.png 300w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/Pam-and-Kelsey-150x150.png 150w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/Pam-and-Kelsey.png 481w\" \/>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-heading heading--5\">\n\t\t\t\t\t\t\t\t\tFenilceton\u00faria (PKU)\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-text\">\n\t\t\t\t\t\t\t\t\tCondi\u00e7\u00e3o metab\u00f3lica rara causada por altera\u00e7\u00f5es na enzima PAH, podendo levar a d\u00e9ficit cognitivo e crises convulsivas quando n\u00e3o tratada adequadamente.\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/a>\n\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide splide__slide\">\n\t\t\t\t\t\t\t<div  class=\"splide__slide__container\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-image\">\n\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"400\" height=\"391\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/01_hATTR-PAF_BEAN-400x391.png\" class=\"attachment-three-up-slider size-three-up-slider\" alt=\"hATTR-PAF Patient\" sizes=\"auto,(min-width: 1920px) calc(1440px \/ 3), (min-width: 1440px) calc(1380px \/ 3), (min-width: 1200px) calc(1140px \/ 3), (min-width: 900px) calc(860px \/ 3), (min-width: 768px) calc(720px \/ 3), (min-width: 600px) calc(540px \/ 2), calc(100vw \/ 1)\" srcset=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/01_hATTR-PAF_BEAN-400x391.png 400w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/01_hATTR-PAF_BEAN-300x293.png 300w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/01_hATTR-PAF_BEAN.png 486w\" \/>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-heading heading--5\">\n\t\t\t\t\t\t\t\t\tAmiloidose heredit\u00e1ria por transtirretina com polineuropatia (hATTR-PN)\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-text\">\n\t\t\t\t\t\t\t\t\tDoen\u00e7a gen\u00e9tica rara e progressiva causada pelo ac\u00famulo de prote\u00ednas anormais (amiloides) nos tecidos, afetando principalmente os nervos perif\u00e9ricos.\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide splide__slide\">\n\t\t\t\t\t\t\t<div  class=\"splide__slide__container\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-image\">\n\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"400\" height=\"346\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/02_SQF-FCS_BEAN-400x346.png\" class=\"attachment-three-up-slider size-three-up-slider\" alt=\"SQF-FCS Patient\" sizes=\"auto,(min-width: 1920px) calc(1440px \/ 3), (min-width: 1440px) calc(1380px \/ 3), (min-width: 1200px) calc(1140px \/ 3), (min-width: 900px) calc(860px \/ 3), (min-width: 768px) calc(720px \/ 3), (min-width: 600px) calc(540px \/ 2), calc(100vw \/ 1)\" srcset=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/02_SQF-FCS_BEAN-400x346.png 400w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/02_SQF-FCS_BEAN-300x260.png 300w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/02_SQF-FCS_BEAN.png 549w\" \/>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-heading heading--5\">\n\t\t\t\t\t\t\t\t\tS\u00edndrome da quilomicronemia familiar (SQF)\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-text\">\n\t\t\t\t\t\t\t\t\tCaracterizada por n\u00edveis extremamente elevados de triglicer\u00eddeos no sangue, podendo causar pancreatites recorrentes e outras complica\u00e7\u00f5es. O controle rigoroso da dieta e o acompanhamento especializado s\u00e3o essenciais.\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide splide__slide\">\n\t\t\t\t\t\t\t<div  class=\"splide__slide__container\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-image\">\n\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"400\" height=\"396\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/03_LPF-FPL_BEAN-400x396.png\" class=\"attachment-three-up-slider size-three-up-slider\" alt=\"LPF-FPL Patient\" sizes=\"auto,(min-width: 1920px) calc(1440px \/ 3), (min-width: 1440px) calc(1380px \/ 3), (min-width: 1200px) calc(1140px \/ 3), (min-width: 900px) calc(860px \/ 3), (min-width: 768px) calc(720px \/ 3), (min-width: 600px) calc(540px \/ 2), calc(100vw \/ 1)\" srcset=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/03_LPF-FPL_BEAN-400x396.png 400w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/03_LPF-FPL_BEAN-300x297.png 300w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/03_LPF-FPL_BEAN-150x150.png 150w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/09\/03_LPF-FPL_BEAN.png 481w\" \/>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-heading heading--5\">\n\t\t\t\t\t\t\t\t\tLipodistrofia parcial familiar (LPF)\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-text\">\n\t\t\t\t\t\t\t\t\tCondi\u00e7\u00e3o metab\u00f3lica rara que leva \u00e0 perda de gordura em regi\u00f5es espec\u00edficas do corpo, n\u00e3o associada a alimenta\u00e7\u00e3o ou gasto de energia, acompanhada por altera\u00e7\u00f5es metab\u00f3licas.\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide splide__slide\">\n\t\t\t\t\t\t\t<div  class=\"splide__slide__container\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-image\">\n\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"400\" height=\"346\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2023\/01\/DMDPatient-400x346.png\" class=\"attachment-three-up-slider size-three-up-slider\" alt=\"DMD Patient\" sizes=\"auto,(min-width: 1920px) calc(1440px \/ 3), (min-width: 1440px) calc(1380px \/ 3), (min-width: 1200px) calc(1140px \/ 3), (min-width: 900px) calc(860px \/ 3), (min-width: 768px) calc(720px \/ 3), (min-width: 600px) calc(540px \/ 2), calc(100vw \/ 1)\" srcset=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2023\/01\/DMDPatient-400x346.png 400w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2023\/01\/DMDPatient-300x260.png 300w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2023\/01\/DMDPatient.png 549w\" \/>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-heading heading--5\">\n\t\t\t\t\t\t\t\t\tDistrofia muscular de Duchenne (DMD)\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-text\">\n\t\t\t\t\t\t\t\t\tDoen\u00e7a gen\u00e9tica rara e progressiva que afeta principalmente meninos, causando enfraquecimento muscular e perda da mobilidade ao longo do tempo.\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide splide__slide\">\n\t\t\t\t\t\t\t<div  class=\"splide__slide__container\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-image\">\n\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"400\" height=\"391\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2023\/01\/aadc-dPatient-400x391.png\" class=\"attachment-three-up-slider size-three-up-slider\" alt=\"AADCd Patient\" sizes=\"auto,(min-width: 1920px) calc(1440px \/ 3), (min-width: 1440px) calc(1380px \/ 3), (min-width: 1200px) calc(1140px \/ 3), (min-width: 900px) calc(860px \/ 3), (min-width: 768px) calc(720px \/ 3), (min-width: 600px) calc(540px \/ 2), calc(100vw \/ 1)\" srcset=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2023\/01\/aadc-dPatient-400x391.png 400w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2023\/01\/aadc-dPatient-300x293.png 300w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2023\/01\/aadc-dPatient.png 486w\" \/>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-heading heading--5\">\n\t\t\t\t\t\t\t\t\tDefici\u00eancia da descarboxilase de L-amino\u00e1cidos arom\u00e1ticos (AADC)\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-text\">\n\t\t\t\t\t\t\t\t\tCondi\u00e7\u00e3o gen\u00e9tica rara que impede a produ\u00e7\u00e3o de dopamina, neurotransmissor essencial para o controle dos movimentos e outras fun\u00e7\u00f5es neurol\u00f3gicas.\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide splide__slide\">\n\t\t\t\t\t\t\t<div  class=\"splide__slide__container\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-image\">\n\t\t\t\t\t\t\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"400\" height=\"349\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/08\/FA-Bean-1-400x349.png\" class=\"attachment-three-up-slider size-three-up-slider\" alt=\"FA Patient\" sizes=\"auto,(min-width: 1920px) calc(1440px \/ 3), (min-width: 1440px) calc(1380px \/ 3), (min-width: 1200px) calc(1140px \/ 3), (min-width: 900px) calc(860px \/ 3), (min-width: 768px) calc(720px \/ 3), (min-width: 600px) calc(540px \/ 2), calc(100vw \/ 1)\" srcset=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/08\/FA-Bean-1-400x349.png 400w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/08\/FA-Bean-1-300x262.png 300w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/08\/FA-Bean-1-1024x894.png 1024w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/08\/FA-Bean-1-768x670.png 768w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2025\/08\/FA-Bean-1.png 1038w\" \/>\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-heading heading--5\">\n\t\t\t\t\t\t\t\t\tAtaxia de Friedreich (FA)\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up-slider__slide-text\">\n\t\t\t\t\t\t\t\t\tDist\u00farbio neuromuscular raro, fisicamente debilitante e que reduz a expectativa de vida, afetando principalmente o sistema nervoso e o cora\u00e7\u00e3o.\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t<\/div>\n\t\t<\/div>\n\t\t\n\t\t\t\t\t\t\t\t\t\t\t\t<a href=\"https:\/\/latam.ptcbio.com\/pt\/areas-terapeuticas\/\" class=\"three-up-slider__cta btn btn--dark-primary\" target=\"_self\">\n\t\t\t\t\tConhe\u00e7a todas as \u00e1reas terap\u00eauticas\t\t\t\t<\/a>\n\t\t\t\t\t\n\t<\/div>\n\n\n\n<div class=\"alignfull wp-block-acf-five-seven-split\">\t<div class=\"five-seven__inner container container--padded container--max-width five-seven__inner--bottom five-seven__inner--right\">\n\t\t<div class=\"five-seven__wrapper\" data-aos=\"\">\n\n\t\t\t\t\t\t\t<div>\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"five-seven__subheading heading--6\">Junte-se ao nosso time<\/div>\n\t\t\t\t\t\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h2 class=\"five-seven__heading heading--2\">Trabalhando como OnePTC<\/h2>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\n\t\t\t\t\t\t\t<div class=\"five-seven__description\"><p><span data-contrast=\"auto\">Como OnePTC, sabemos da urg\u00eancia em ajudar aqueles com necessidades m\u00e9dicas significativas n\u00e3o atendidas. Estamos motivados a oferecer solu\u00e7\u00f5es e novas possibilidades para nossos pacientes.<\/span><span data-ccp-props=\"{}\">\u00a0<\/span><\/p>\n<p><span data-contrast=\"auto\">Fazer coisas que ningu\u00e9m jamais fez \u00e9 dif\u00edcil. Mas isso n\u00e3o nos desanima. Somos apaixonados pelo que fazemos.<\/span><span data-ccp-props=\"{}\">\u00a0<\/span><\/p>\n<p><span data-contrast=\"auto\">Se voc\u00ea busca um trabalho com prop\u00f3sito e colegas inspiradores, venha crescer com a gente.<\/span><span data-ccp-props=\"{}\">\u00a0<\/span><\/p>\n<\/div>\n\t\t\t\n\t\t\t\n\t\t\t\t<div class=\"dual-cta__ctas dual-cta__ctas--same dual-cta__ctas--left\">\n\n\t\t\t\t\t<a href=\"https:\/\/www.ptcbio.com\/careers\" target=\"_blank\" class=\"dual-cta__button btn btn--dark-primary\">Conhe\u00e7a as oportunidades na PTC<\/a>\n\t\t\n\t\t\n\t\t\n\t<\/div>\n\t\t<\/div>\n\n\t\t\t\t\t<div class=\"five-seven__image-outer\" >\n\t\t\t<img loading=\"lazy\" decoding=\"async\" width=\"768\" height=\"384\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2024\/07\/Lab_Employees2024-768x384.png\" class=\"five-seven__image\" alt=\"PTC Lab Employees\" sizes=\"auto, (min-width: 1920px) 836px, (min-width: 1440px) 801px, (min-width: 1200px) 662px, (min-width: 900px) 499px, (min-width: 768px) 720px, (min-width: 600px) 540px, 100vw\" srcset=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2024\/07\/Lab_Employees2024-768x384.png 768w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2024\/07\/Lab_Employees2024-300x150.png 300w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2024\/07\/Lab_Employees2024-1024x512.png 1024w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2024\/07\/Lab_Employees2024-1536x769.png 1536w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2024\/07\/Lab_Employees2024-2048x1025.png 2048w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2024\/07\/Lab_Employees2024-400x200.png 400w, https:\/\/latam.ptcbio.com\/pt\/wp-content\/uploads\/sites\/10\/2024\/07\/Lab_Employees2024-1920x960.png 1920w\" \/>\t\t\t<\/div>\n\t\t\t<\/div>\n\n\t<\/div>\n\n\n\n\t<div  class=\"three-up background-color--violet color-theme--white\">\n\t<div class=\"wave-background\">\n\t<svg version=\"1.1\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" xmlns:xlink=\"http:\/\/www.w3.org\/1999\/xlink\" x=\"0px\" y=\"0px\" viewBox=\"0 0 1920 500\" style=\"background-color: var( --wp--preset--color--white );\" xml:space=\"preserve\">\n\t\t<path class=\"wave-fill\" fill=\"var( --wp--preset--color--violet )\" d=\"M1920,74.15c-38.59-2.24-174.99,5.85-201.25,7.94c-712.52,56.21-622.97,28.51-985.12-23.62\n\t\t\tC383.51,8.07,23.55,72.63,0,76.98V500h1920V74.15z\"\/>\n\t<\/svg>\n<\/div>\n\n<div class=\"wave-background wave-background--top\">\n\t<svg data-name=\"Layer 1\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" viewBox=\"0 0 414.6 278.62\">\n\t\t<path class=\"wave-fill\" fill=\"var( --wp--preset--color--white )\" d=\"M0,0V275.24s65.05-40.81,260.26-9.88c0,0,87.7,21.31,154.34,9.88V0H0Z\"\/>\n\t<\/svg>\n<\/div>\n\n\n\t<div class=\"three-up__content-blocks three-up__content-blocks--has-icons\" >\n\t\t\t\t\t<div class=\"three-up__content-block\">\n\n\t\t\t\t\t\t\t\t\t<img decoding=\"async\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/themes\/ptc-redesign\/images\/bean-stethoscope--thin.svg\" alt=\"\">\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up__content-block-subheading heading--6\">\n\t\t\t\t\t\tApoio\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t<div class=\"three-up__content-block-heading heading--4\">\n\t\t\t\t\tPara profissionais de sa\u00fade\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t<div class=\"three-up__content-block-text\">\n\t\t\t\t\t\t<p>A PTC atua lado a lado com profissionais de sa\u00fade para atender \u00e0s suas necessidades.<\/p>\n\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up__content-block-link\">\n\t\t\t\t\t\t<a href=\"https:\/\/www.ptcbio.com\/healthcare-providers-resources\/\" class=\"text-cta text-cta--secondary\" target=\"\">Saiba como<\/a>\n\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t<div class=\"three-up__content-block\">\n\n\t\t\t\t\t\t\t\t\t<img decoding=\"async\" src=\"https:\/\/latam.ptcbio.com\/pt\/wp-content\/themes\/ptc-redesign\/images\/bean-chart-arrow--thin.svg\" alt=\"\">\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up__content-block-subheading heading--6\">\n\t\t\t\t\t\tInforma\u00e7\u00f5es para\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t<div class=\"three-up__content-block-heading heading--4\">\n\t\t\t\t\tInvestidores\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t<div class=\"three-up__content-block-text\">\n\t\t\t\t\t\t<p>Explore nossa \u00e1rea de rela\u00e7\u00f5es com investidores e cadastre-se para receber atualiza\u00e7\u00f5es e novidades importantes.<\/p>\n\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"three-up__content-block-link\">\n\t\t\t\t\t\t<a href=\"https:\/\/ir.ptcbio.com\/email-alerts\" class=\"text-cta text-cta--secondary\" target=\"_blank\">Receba novidades por e-mail<\/a>\n\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t<\/div>\n\t\t\t<\/div>\n<\/div>\n\n","protected":false},"excerpt":{"rendered":"","protected":false},"author":14,"featured_media":0,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_acf_changed":false,"footnotes":""},"class_list":["post-10486","page","type-page","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO Premium plugin v27.2 (Yoast SEO v27.2) - https:\/\/yoast.com\/product\/yoast-seo-premium-wordpress\/ -->\n<title>PTC Therapeutics | Pioneers in Rare Disease Treatments<\/title>\n<meta name=\"description\" content=\"PTC Therapeutics pioneers pharmaceutical science to transform lives and treat rare diseases, like Duchenne Muscular Dystrophy, Spinal Muscular Atrophy, Huntington&#039;s Disease, Leukemia, and more.\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link 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